Proof-of-concept for a gene replacement approach to CDKL5 deficiency disorder

TA Benke, PC Kind - Brain, 2020 - academic.oup.com
TA Benke, PC Kind
Brain, 2020academic.oup.com
Proof-of-concept for a gene replacement approach to CDKL5 deficiency disorder | Brain |
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This scientific commentary refers to ‘Gene replacement ameliorates deficits in mouse and human models of cyclin-dependent kinase-like 5 disorder’, by Gao etal. (doi:10.1093/brain/awaa028).
Oxford University Press