Lys05: a new lysosomal autophagy inhibitor

RK Amaravadi, JD Winkler - Autophagy, 2012 - Taylor & Francis
Autophagy, 2012Taylor & Francis
Lys05 is a previously undescribed dimeric chloroquine which more potently accumulates in
the lysosome and blocks autophagy compared with HCQ. Lys05 produced more potent
antitumor activity as a single agent both in vitro and in vivo in multiple human cancer cell
lines and xenograft models compared with HCQ. Initial structure-activity relationship studies
demonstrated that the increased activity associated with Lys05 was due to the bivalent
aminoquinoline rings, C7-Chlorine, and a short triamine linker. While lower doses of Lys05 …
Lys05 is a previously undescribed dimeric chloroquine which more potently accumulates in the lysosome and blocks autophagy compared with HCQ. Lys05 produced more potent antitumor activity as a single agent both in vitro and in vivo in multiple human cancer cell lines and xenograft models compared with HCQ. Initial structure-activity relationship studies demonstrated that the increased activity associated with Lys05 was due to the bivalent aminoquinoline rings, C7-Chlorine, and a short triamine linker. While lower doses of Lys05 were well tolerated and associated with antitumor activity, at the highest dose tested, Lys05 produced Paneth cell dysfunction and intestinal toxicity, similar to what can be observed in mice and humans with genetic defects in the autophagy gene ATG16L1. Lys05 is therefore a new lysosomal autophagy inhibitor that has potential to be developed further into a drug for cancer and other medical applications.
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