Adenosine deaminase (ADA) deficiency is a disorder of purine salvage that has its most
devastating consequences in the immune system leading to severe combined
immunodeficiency (SCID). Management options for ADA SCID include hematopoietic stem
cell transplantation, enzyme replacement therapy and gene therapy. Formal data on the
outcome following each of the three treatment modalities are limited, and this symposium
was held in order to gather together the experience from major centers in Europe and the …